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Impact of Friedreich Ataxia on Quality of Life
Sub Subramony, M.D., discusses how the progression of patients' conditions often leads to a decline in quality of life and functional capabilities, highlighting key clinical indicators that necessitate the adoption of mobility aids.
EP: 1.Friedreich Ataxia: Addressing Treatment Objectives and Comorbidities
EP: 2.Guidelines & FDA Approval of Novel Friedreich Ataxia Therapy
EP: 3.Engaging mFARS Scale to Monitor Friedreich Ataxia Progression
EP: 4.Managing Adverse Events in Novel Friedreich’s Ataxia Therapy
EP: 5.Examining Trial Data on Omaveloxolone Efficacy
EP: 6.Promising Therapy Approaches for Advanced Friedreich Ataxia
EP: 7.Friedreich Ataxia: Looking Forward at the Treatment Landscape
EP: 8.Epidemiology, Pathophysiology, and Symptomatology of Friedreich Ataxia
EP: 9.Diagnosis of Friedreich Ataxia
EP: 10.Impact of Friedreich Ataxia on Quality of Life
EP: 11.Clinical Utility of the Modified Friedreich Ataxia Rating Scale
EP: 12.Comorbidities and Complications Associated With Friedreich Ataxia
EP: 13.Challenges Associated With Friedreich Ataxia
EP: 14.Future Considerations for Friedreich Ataxia
Video content above is prompted by the following:
Can you shed light on the trajectory of patients’ quality of life, functional capabilities, and overall well-being as the condition advances, and how do you typically discern indications in clinical settings that signal a decline in ambulation necessitating the adoption of mobility aids?
WVE-N531 Shows Promising Efficacy in DMD at Interim FORWARD-53 Analysis
September 26th 2024In the phase 2 FORWARD-53 study, the exon-skipping oligonucleotide WVE-N531 showed promising safety and efficacy in boys with Duchenne muscular dystrophy (DMD) who are amenable to exon 53 skipping.
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