Officials Revise Goals on Containing Ebola After Signs of Wider Exposure in Mali

Onasemnogene abeparvovec-brve is now the first gene replacement therapy approved for spinal muscular atrophy in patients 2 years and older.

On this episode of Managed Care Cast, we're talking with the chief science officer of the Center for Innovation & Value Research about key insights from its Rare Disease project.

Three researchers received the 2025 Nobel Prize in Physiology or Medicine for discovering regulatory T cells and the Foxp3 gene, which revealed how the immune system prevents autoimmune disease.

Shereef Elnahal, MD, MBA, under secretary for health at the Veterans Health Administration (VHA), sat for a conversation with our hosts Emeline Aviki, MD, MBA, Memorial Sloan Kettering Cancer Center, and Stephen Schleicher, MD, MBA, Tennessee Oncology, that covered the cancer footprint of the VHA.

Evinacumab-dgnb approval expands treatment options for children with homozygous familial hypercholesterolemia (HoFH).

David Mitchell, PharmD, MBA, senior pharmacist manager and assistant clinical professor at UC Davis, addresses how health systems are overcoming financial, operational, and access challenges for patients with rare diseases.